Therapeutics

Tools

Back to the Top
Search By Attributes

Search Results

Name Synonyms FDA Status Company Target Type Therapy Type Approved
For
AAVrh.10-APOE2 AAVrh.10hAPOE2 Alzheimer's Disease (Phase 1) Amyloid-Related DNA/RNA-based
BIIB080 IONIS-MAPTRx,
ISIS 814907
Alzheimer's Disease (Phase 1) Biogen, IONIS Pharmaceuticals Tau DNA/RNA-based
BIIB094 ION859,
IONIS-BIIB7Rx
Parkinson's Disease (Phase 1) Biogen, IONIS Pharmaceuticals Inflammation, Other DNA/RNA-based
CERE-110 Nerve Growth Factor gene therapy Alzheimer's Disease (Discontinued) Sangamo BioSciences, Inc. Other DNA/RNA-based
PR001 PR001A Parkinson's Disease (Phase 1/2) Prevail Therapeutics Other DNA/RNA-based
Tofersen BIIB067,
Ionis-SOD1Rx,
ASO1
Amyotrophic Lateral Sclerosis (Phase 3) Biogen, IONIS Pharmaceuticals Other DNA/RNA-based
VY-AADC VY-AADC01,
VY-AADC02
Parkinson's Disease (Phase 2) Neurocrine Biosciences, Voyager Therapeutics Other Neurotransmitters DNA/RNA-based